Search GLEAM-DB / CoGenEx-PM3

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Input query
Recognized gene
ATM, ATP6V1B1, B3GALT6, BIN1, CC2D2A and 31 more
Normalized c.HGVS
c.-32-13T>G, c.10102G>A, c.1103G>T, c.1294G>A, c.1366C>T and 43 more
Normalized p.HGVS
p.(=), p.(Ala182Thr), p.(Ala220Ser), p.(Ala2753Thr), p.(Ala3190Val) and 41 more
Matching records
4816
PM3-positive records
293

Results are ordered by PM3-relevant evidence first. Reviewed source only indicates whether main text, supplementary material, or both were reviewed; it is not the evidence conclusion.

Download current query results as TSV
Gene Variant Evidence PM3 context Publication Reviewed source Actions
GNE NM_005476.7:c.1259G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.416_426del; p.Ile139Argfs*4
context: Confirmed in trans
34858435
Severe Congenital Thrombocytopenia Characterized by Decreased Platelet Sialylation and Moderate Complement Activation Caused by Novel Compound Heterozygous Variants in GNE.
Frontiers in immunology, 2021
Main article
Open
SCO2 NM_005138.3:c.179G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.577G>A; p.(Gly193Ser)
context: Confirmed in trans
34746378
Adult Cerebellar Ataxia, Axonal Neuropathy, and Sensory Impairments Caused by Biallelic SCO2 Variants.
Neurology. Genetics, 2021
Main article
Open
ATM NM_000051.4:c.9156G>T Phase-confirmed PM3 evidence
Low confidence
Homozygous for query variant
context: Confirmed in trans
34728979
Abnormal Saccades Differentiate Adolescent Onset Variant Ataxia Telangiectasia from Other Myoclonus Dystonia.
Annals of Indian Academy of Neurology, 2021
Main article
Open
WDR62 NM_001083961.2:c.3878C>A Phase-confirmed PM3 evidence
High confidence
PM3 evidence identified; partner variant not structured
context: Confirmed in trans
34728968
Association of Infantile Spasms and Hypsarrhythmia with Primary Microcephaly- Three Case Reports.
Annals of Indian Academy of Neurology, 2021
Main article
Open
DARS2 NM_018122.5:c.508C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.228‐16C>A
context: Confirmed in trans
34631948
Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation: A Novel DARS2 Mutation and Intra-Familial Heterogeneity.
Movement disorders clinical practice, 2021
Main article
Open
LAMA2 NM_000426.4:c.7681G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.4840A>G; p.Asn1614Asp
context: Confirmed in trans
34528292
Identification of a compound heterozygous missense mutation in LAMA2 gene from a patient with merosin-deficient congenital muscular dystrophy type 1A.
Journal of clinical laboratory analysis, 2021
Main article
Open
TBC1D24 NM_001199107.2:c.643T>G Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.641G > A; p.(Arg214His)
context: Confirmed in trans
34440452
Benefits of Exome Sequencing in Children with Suspected Isolated Hearing Loss.
Genes, 2021
Main article
Open
PIEZO1 NM_001142864.4:c.4027GAG[1] Phase-confirmed PM3 evidence
Not assessed
Confirmed in trans with c.3895C > T; p.R1299C
context: Confirmed in trans
34421994
Case Report: Whole Exome Sequencing Revealed Two Novel Mutations of PIEZO1 Implicated in Nonimmune Hydrops Fetalis.
Frontiers in genetics, 2021
Main article
Open
DCLRE1C NM_001033855.3:c.632G>C Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with deletion in exons 1–3
context: Confirmed in trans
34420125
Self-Limited COVID-19 in a Patient with Artemis Hypomorphic SCID.
Journal of clinical immunology, 2021
Main article
Open
LZTR1 NM_006767.4:c.988A>G Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.594‐3C>T
context: Confirmed in trans
34401172
Spontaneous resolution of nonimmune hydrops fetalis in a fetus with TP63 gene mutation and LZTR1 gene variants.
Clinical case reports, 2021
Main article
Open
PYGM NM_005609.4:c.389C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.415 C>T; c.415C>T; R139W; +1 more
context: Confirmed in trans
34373715
Molecular diagnosis of McArdle disease using whole-exome sequencing.
Experimental and therapeutic medicine, 2021
Main article
Open
IKBKB NM_001556.3:c.1676C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1552G>A; p.D518K
context: Confirmed in trans
33822308
Selected Abstracts from the 12(th) Annual Meeting of the Clinical Immunology Society: 2021 Virtual Annual Meeting: Immune Deficiency and Dysregulation North American Conference.
Journal of clinical immunology, 2021
Main article
Open
TSFM NM_005726.6:c.161G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.919C > T; p.Gln307*
context: Confirmed in trans
33816677
Novel Mutation in the TSFM Gene Causes an Early-Onset Complex Chorea without Basal Ganglia Lesions.
Movement disorders clinical practice, 2021
Main article
Open
ACD NM_001082486.2:c.1213C>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.508_510del; p.(Lys170del)
context: Confirmed in trans
33446513
Identification and characterization of novel ACD variants: modulation of TPP1 protein level offsets the impact of germline loss-of-function variants on telomere length.
Cold Spring Harbor molecular case studies, 2021
Main article
Open
WDR35 NM_020779.4:c.308G>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1633C > T; p.(Arg545*)
context: Confirmed in trans
33369054
Ciliopathies: Coloring outside of the lines.
American journal of medical genetics. Part A, 2021
Main article
Open
PKD1 NM_001009944.3:c.11675G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.11876C>T; Arg3959Val; p.(Ala3959Val)
context: Confirmed in trans
33168999
Biallelic inheritance of hypomorphic PKD1 variants is highly prevalent in very early onset polycystic kidney disease.
Genetics in medicine : official journal of the American College of Medical Genetics, 2021
Main article
Open
PKD1 NM_001009944.3:c.8998C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.3739A>G; p.(Met1247Val)
context: Confirmed in trans
33168999
Biallelic inheritance of hypomorphic PKD1 variants is highly prevalent in very early onset polycystic kidney disease.
Genetics in medicine : official journal of the American College of Medical Genetics, 2021
Main article
Open
FARS2 NM_006567.5:c.323C>T Phase-unconfirmed biallelic evidence
Needs review
Possible compound heterozygous with p.D265TfsX29; p.D62N
context: Compound heterozygous candidate
36531778
FARS2 (Phenylalanyl-tRNA Synthetase 2) Deficiency: A Novel Mutation Associated with EEG Phenotype of Epilepsy of Infancy with Migrating Focal Seizures (EIMFS).
Journal of pediatric neurosciences, 2021
Main article
Open
NDUFS3 NM_004551.3:c.418C>T Phase-unconfirmed biallelic evidence
Needs review
Possible compound heterozygous with R199W
context: Compound heterozygous candidate
36531773
Mitochondrial Ultrastructural Defects in NDUFS3-Related Disorder.
Journal of pediatric neurosciences, 2021
Main article
Open
RLBP1 NM_000326.5:c.361C>T Phase-unconfirmed biallelic evidence
High confidence
Confirmed in trans with c.677T>A; p.Met226Lys
context: Confirmed in trans
36247817
Retinitis Punctata Albescens and RLBP1-Allied Phenotypes: Phenotype-Genotype Correlation and Natural History in the Aim of Gene Therapy.
Ophthalmology science, 2021
Main article
Open