Search GLEAM-DB / CoGenEx-PM3

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Input query
Recognized gene
AARS1, AARS2, AASS, ABAT, ABCA3 and 1 more
Normalized c.HGVS
c.*1251G>A, c.*718C>A, c.-103C>G, c.-154G>A, c.-279G>A and 44 more
Normalized p.HGVS
p.(=), p.(Arg1425His), p.(Arg1457Gln), p.(Arg320Cys), p.(Arg320Gly) and 33 more
Matching records
9119
PM3-positive records
293

Results are ordered by PM3-relevant evidence first. Reviewed source only indicates whether main text, supplementary material, or both were reviewed; it is not the evidence conclusion.

Download current query results as TSV
Gene Variant Evidence PM3 context Publication Reviewed source Actions
SLC6A19 NM_001003841.3:c.1522G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.47C>T; P16L
context: Confirmed in trans
33817063
Study of Seizure-Manifested Hartnup Disorder Case Induced By Novel Mutations in SLC6A19.
Open life sciences, 2018
Main article
Open
POMGNT1 NM_017739.4:c.461C>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.550C>T; p.His184Tyr
context: Confirmed in trans
30937090
Congenital Muscular Dystrophy due to Novel Compound Heterozygote Mutations in POMGNT1 Gene.
Journal of pediatric neurosciences, 2018
Main article
Open
POMGNT1 NM_017739.4:c.550C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.461C>A; p.Pro154His
context: Confirmed in trans
30937090
Congenital Muscular Dystrophy due to Novel Compound Heterozygote Mutations in POMGNT1 Gene.
Journal of pediatric neurosciences, 2018
Main article
Open
PKD1 NM_001009944.3:c.9313C>T Phase-confirmed PM3 evidence
Needs review
Confirmed in trans with Arg2765Cys
context: Confirmed in trans
30647506
Autosomal Dominant Polycystic Kidney Disease: Presence of Hypomorphic Alleles in PKD1 Gene.
Indian journal of nephrology, 2018
Main article
Open
CACNA2D2 NM_006030.4:c.782C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.3137T>C; p.Leu1046Pro
context: Confirmed in trans
30410802
Epileptic Encephalopathy and Cerebellar Atrophy Resulting from Compound Heterozygous CACNA2D2 Variants.
Case reports in genetics, 2018
Main article
Open
ELAC2 NM_018127.7:c.394G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1040C>T; p.Ser347Phe
context: Confirmed in trans
30217939
Chorea, psychosis, acanthocytosis, and prolonged survival associated with ELAC2 mutations.
Neurology, 2018
Main article
Open
SLC26A4 NM_000441.2:c.-103T>C Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.-66C>G
context: Confirmed in trans
30068397
Contribution of SLC26A4 to the molecular diagnosis of nonsyndromic prelingual sensorineural hearing loss in a Brazilian cohort.
BMC research notes, 2018
Main article
Open
SEC23B NM_006363.6:c.1831C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1352G>T; p.C451F
context: Confirmed in trans
30032575
[Congenital dyserythropoietic anemia type Ⅱ with rare SEC23B mutations: a case report].
Zhonghua xue ye xue za zhi = Zhonghua xueyexue zazhi, 2018
Main article
Open
TRAPPC11 NM_021942.6:c.965+5G>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.851A>C; p.Q284P
context: Confirmed in trans
29855340
TRAPPC11 and GOSR2 mutations associate with hypoglycosylation of α-dystroglycan and muscular dystrophy.
Skeletal muscle, 2018
Main article
Open
DNAH9 NM_001372.4:c.6431G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.2968; R/C; R990C
context: Confirmed in trans
29738522
De novo and inherited private variants in MAP1B in periventricular nodular heterotopia.
PLoS genetics, 2018
Supplementary material
Open
BBS12 NM_152618.3:c.1156C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.56T>G; p.Leu19Arg
context: Confirmed in trans
29633607
Identification of A Novel Compound Heterozygous Mutation in BBS12 in An Iranian Family with Bardet-Biedl Syndrome Using Targeted Next Generation Sequencing.
Cell journal, 2018
Main article
Open
RYR1 NM_000540.3:c.178G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.10817T>C; p.L3606P
context: Confirmed in trans
29629541
Clinical and Pathologic Findings of Korean Patients with RYR1-Related Congenital Myopathy.
Journal of clinical neurology (Seoul, Korea), 2018
Main article
Open
CDAN1 NM_138477.4:c.1003C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.2174G>A; p.Arg725Gln
context: Confirmed in trans
29599085
Fetal presentation of congenital dyserythropoietic anemia type 1 with novel compound heterozygous CDAN1 mutations.
Blood cells, molecules & diseases, 2018
Main article
Open
TNFRSF13B NM_012452.3:c.365G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.452C>T; p.P151L
context: Confirmed in trans
29531467
Phenotypic and genotypic characterization of inflammatory bowel disease in children under six years of age in China.
World journal of gastroenterology, 2018
Main article
Open
TNFRSF13B NM_012452.3:c.452C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.365G>A; p.R122Q
context: Confirmed in trans
29531467
Phenotypic and genotypic characterization of inflammatory bowel disease in children under six years of age in China.
World journal of gastroenterology, 2018
Main article
Open
LZTR1 NM_006767.4:c.2089C>T Phase-confirmed PM3 evidence
Needs review
Confirmed in trans with c.2407-2A>G
context: Confirmed in trans
29469822
Autosomal recessive Noonan syndrome associated with biallelic LZTR1 variants.
Genetics in medicine : official journal of the American College of Medical Genetics, 2018
Supplementary material
Open
POLR3A NM_007055.4:c.200G>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.2722G>T; p.D908Y
context: Confirmed in trans
29451896
Hypomyelinating disorders in China: The clinical and genetic heterogeneity in 119 patients.
PloS one, 2018
Main article
Open
MTHFR NM_005957.5:c.1162C>T Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1970G > C; p.(*657Serext*50); stop-loss
context: Confirmed in trans
29391032
Adolescence/adult onset MTHFR deficiency may manifest as isolated and treatable distinct neuro-psychiatric syndromes.
Orphanet journal of rare diseases, 2018
Main article
Open
GBE1 NM_000158.4:c.2056T>C Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1570C>T; Arg524*; p.(Arg524*); +1 more
context: Confirmed in trans
29379554
Variable clinical presentation of glycogen storage disease type IV: from severe hepatosplenomegaly to cardiac insufficiency. Some discrepancies in genetic and biochemical abnormalities.
Archives of medical science : AMS, 2018
Main article
Open
SLC26A4 NM_000441.2:c.1301C>A Phase-confirmed PM3 evidence
High confidence
Confirmed in trans with c.1730T>C; p.V577A
context: Confirmed in trans
29320412
Functional Testing of SLC26A4 Variants-Clinical and Molecular Analysis of a Cohort with Enlarged Vestibular Aqueduct from Austria.
International journal of molecular sciences, 2018
Main article
Open